ARTICLE | Distillery Therapeutics
Therapeutics: Ubiquitin protein ligase E3A (UBE3A; E6AP)
January 8, 2015 8:00 AM UTC
In vitro and mouse studies suggest an antisense oligonucleotide (ASO) against UBE3A-ATS - a long noncoding RNA UBE3A antisense transcript - could help treat Angelman syndrome. The disease is caused by...