BioCentury
ARTICLE | Clinical News

Spark completes rolling BLA submission for voretigene neparvovec

May 26, 2017 7:40 PM UTC

Spark Therapeutics Inc. (NASDAQ:ONCE) completed submission of a rolling BLA to FDA for voretigene neparvovec (AAV2-hRPE65v2) to treat patients with vision loss due to confirmed, biallelic, retinal pi...

Get Unlimited Access
Continue reading with a free trial.
Or Purchase This Article