ARTICLE | Clinical News
Spark completes rolling BLA submission for voretigene neparvovec
May 26, 2017 7:40 PM UTC
Spark Therapeutics Inc. (NASDAQ:ONCE) completed submission of a rolling BLA to FDA for voretigene neparvovec (AAV2-hRPE65v2) to treat patients with vision loss due to confirmed, biallelic, retinal pi...
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