ARTICLE | Product Development
The extraordinary journey that led to a new Pompe treatment
Hollywood dramatized development of the first Pompe medicine; the sequel would be more exciting
October 9, 2023 5:34 PM UTC
John Crowley’s role in creating a medicine that helped his two young children survive after being diagnosed with Pompe disease was so poignant that it was dramatized in a Hollywood movie, Extraordinary Measures. The story that came after that was even more dramatic.
The film followed the path that led to creation of the first enzyme replacement therapy for Pompe, Lumizyme/Myozyme alglucosidase alfa from Sanofi (Euronext:SAN; NASDAQ:SNY). ...