Visgenx: Taking retinal gene therapy beyond rare disease
First program delivers an enzyme involved in the fatty acid synthesis pathway for patients with dry AMD
Visgenx is delivering a gene therapy to restore expression of an enzyme involved in a fatty acid pathway that the company believes could slow or stop progressive vision loss in patients with age-related macular degeneration.
The strategy represents a departure from the more common use of gene therapy — to deliver a functional copy of a gene that’s mutated in a rare and severe genetic disorder. ...
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